Reaching, Enrolling, & Retaining Participants in Rare Disease Clinical Trials
Time: 8:31 am
day: Workshop D
Details:
- Dissecting real-world examples to prepare for the length and ambition of studies
- Evolving strategies to identify patients for rare disease clinical trials: Using electronic health records (EHRs) to identify computable phenotypes and conduct life-course research
- Discussing friction points and strategy for pharmacological interventions, as well as combination trials alongside preexisting patient care, and gene therapies
- Working with private physicians and Centres of Excellence for patient recruitment
