Welcome to the 4th Rare & Genetic Kidney Disease Drug Development Summit
With recent accelerated approval wins, positive clinical trial readouts, progression through clinical pipelines and exciting mergers and acquisitions, it has certainly been an industry-defining year for the rare and genetic renal space.
In the context of rapid progress and a mounting desire to propel game-changing novel therapies that will add to the arsenal of therapeutic options for patients, the 4th Rare & Genetic Kidney Disease Drug Development Summit returned to Boston. This unique event for the industry, academic KOL, and patient advocacy nephrology community provided an unrivalled opportunity to discuss acceleration of clinical advancements in orphan kidney disease populations.
2024's meeting brought together 30+ expert speakers, a two-tracked pre-conference workshop day and new content on podocyte biology, tissue bioengineering of kidney tissue models, market access strategies, as well as pricing and reimbursement conversations, across a breadth of rare renal therapeutic areas including FSGS, PKD, Alport Syndrome and IgAN to name but a few!
The 4th Rare & Genetic Kidney Disease Drug Development Summit was your most comprehensive opportunity for learning about the latest preclinical and clinical progress. Peers joined to address the unique challenges of rare renal drug development to spearhead novel therapeutics through to regulatory approval.
What Did You Miss From 2024:
Spanning discovery through to trial development and market access, this end-to-end summit discussed challenges and opportunities from:
Exploring molecular intricacies underlying disease pathophysiology
Uncovering genetic study and -omic profiles to map response profiles and biomarkers
Evolving new strategies for patient identification using electronic health records, applying patient-centric outcome measures in trial design
Working with patients and associations as partners
Whether you’re entering the rare and genetic renal space or are a well-seasoned nephrology veteran, this forum equipped you with the know-how and connections to make rapid advances in your work.